X Chromosome Therapies: A Breakthrough for Genetic Disorders

April 7, 2025

X chromosome therapies represent a groundbreaking advancement in the treatment of genetic diseases, particularly X-linked disorders like Fragile X Syndrome and Rett Syndrome.These innovative approaches aim to undo the complexities of chromosome inactivation, a process that affects one of the two X chromosomes in females, leading to the inactivation of vital genes.
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